Why rare diseases are an important medical and social issue

Lancet. 2008 Jun 14;371(9629):2039-41. doi: 10.1016/S0140-6736(08)60872-7.
No abstract available

Publication types

  • Review

MeSH terms

  • Humans
  • Orphan Drug Production / legislation & jurisprudence*
  • Prevalence
  • Quality of Life
  • Rare Diseases / drug therapy
  • Rare Diseases / epidemiology*
  • Rare Diseases / genetics
  • Social Responsibility*
  • United States