PMC Links for Gene (Select 14071) - PMC

Links from Gene

Items: 1 to 20 of 48

<< First< Prev

Page of 3

Next >Last >>

Select item 60783541.

Coagulation factor 9-deficient mice are protected against dextran sulfate sodium-induced colitis

Avinash Khandagale, Jens M. Kittner, Amrit Mann, Stefanie Ascher, Bettina Kollar, Christoph Reinhardt

Biol Open. 2018 Jul 15; 7(7): bio034140. Published online 2018 Jun 26. doi: 10.1242/bio.034140

PMCID:: PMC6078354

Article PDF–1.0M

Select item 56663102.

Genome editing for scalable production of alloantigen‐free lentiviral vectors for in vivo gene therapy

Michela Milani, Andrea Annoni, Sara Bartolaccini, Mauro Biffi, Fabio Russo, Tiziano Di Tomaso, Andrea Raimondi, Johannes Lengler, Michael C Holmes, Friedrich Scheiflinger, Angelo Lombardo, Alessio Cantore, Luigi Naldini

EMBO Mol Med. 2017 Nov; 9(11): 1558–1573. Published online 2017 Aug 23. doi: 10.15252/emmm.201708148

PMCID:: PMC5666310

Article PDF–1.5M

Select item 53916233.

Abnormal joint and bone wound healing in hemophilia mice is improved by extending factor IX activity after hemarthrosis

Junjiang Sun, Baolai Hua, Eric W. Livingston, Sarah Taves, Peter B. Johansen, Maureane Hoffman, Mirella Ezban, Dougald M. Monroe, Ted A. Bateman, Paul E. Monahan

Blood. 2017 Apr 13; 129(15): 2161–2171. Prepublished online 2016 Dec 30. doi: 10.1182/blood-2016-08-734053

PMCID:: PMC5391623

Article

Select item 53475964.

Systemic delivery of factor IX messenger RNA for protein replacement therapy

Suvasini Ramaswamy, Nina Tonnu, Kiyoshi Tachikawa, Pattraranee Limphong, Jerel B. Vega, Priya P. Karmali, Pad Chivukula, Inder M. Verma

Proc Natl Acad Sci U S A. 2017 Mar 7; 114(10): E1941–E1950. Published online 2017 Feb 15. doi: 10.1073/pnas.1619653114

PMCID:: PMC5347596

Article PDF–1.4M

Select item 52913015.

Prophylactic efficacy of BeneFIX vs Alprolix in hemophilia B mice

Brian Cooley, William Funkhouser, Dougald Monroe, Ashley Ezzell, David M. Mann, Feng-Chang Lin, Paul E. Monahan, Darrel W. Stafford

Blood. 2016 Jul 14; 128(2): 286–292. Prepublished online 2016 Apr 22. doi: 10.1182/blood-2016-01-696104

PMCID:: PMC5291301

Article

Select item 51258326.

CRISPR/Cas9‐mediated somatic correction of a novel coagulator factor IX gene mutation ameliorates hemophilia in mouse

Yuting Guan, Yanlin Ma, Qi Li, Zhenliang Sun, Lie Ma, Lijuan Wu, Liren Wang, Li Zeng, Yanjiao Shao, Yuting Chen, Ning Ma, Wenqing Lu, Kewen Hu, Honghui Han, Yanhong Yu, Yuanhua Huang, Mingyao Liu, Dali Li

EMBO Mol Med. 2016 May; 8(5): 477–488. Published online 2016 Mar 10. doi: 10.15252/emmm.201506039

PMCID:: PMC5125832

Article PDF–1.9M

Select item 44922007.

Hemostatic agents of broad applicability produced by selective tuning of factor Xa zymogenicity

Lacramioara Ivanciu, Rodney M. Camire

Blood. 2015 Jul 2; 126(1): 94–102. Prepublished online 2015 Apr 20. doi: 10.1182/blood-2015-03-634329

PMCID:: PMC4492200

Article

Select item 43920108.

Plant-based oral tolerance to hemophilia therapy employs a complex immune regulatory response including LAP⁺CD4⁺ T cells

Xiaomei Wang, Jin Su, Alexandra Sherman, Geoffrey L. Rogers, Gongxian Liao, Brad E. Hoffman, Kam W. Leong, Cox Terhorst, Henry Daniell, Roland W. Herzog

Blood. 2015 Apr 9; 125(15): 2418–2427. Prepublished online 2015 Feb 19. doi: 10.1182/blood-2014-08-597070

PMCID:: PMC4392010

Article

Select item 43095089.

Immune responses to human factor IX in haemophilia B mice of different genetic backgrounds are distinct and modified by TLR4

B K Sack, X Wang, A Sherman, G L Rogers, D M Markusic

Haemophilia. 2015 Jan; 21(1): 133–139. Published online 2014 Nov 23. doi: 10.1111/hae.12522

PMCID:: PMC4309508

Article PDF–344K

Select item 430948810.

Novel, high incidence exercise-induced muscle bleeding model in hemophilia B mice: rationale, development and prophylactic intervention

M Tranholm, A T Kristensen, M L Broberg, M P Groth

J Thromb Haemost. 2015 Jan; 13(1): 82–91. Published online 2014 Dec 11. doi: 10.1111/jth.12775

PMCID:: PMC4309488

Article PDF–638K

Select item 429759811.

Promoterless gene targeting without nucleases ameliorates haemophilia B in mice

A. Barzel, N.K. Paulk, Y. Shi, Y. Huang, K. Chu, F. Zhang, P.N. Valdmanis, L.P. Spector, M.H. Porteus, K.M. Gaensler, M.A. Kay

Nature. Author manuscript; available in PMC 2015 Jul 15.

Published in final edited form as: Nature. 2015 Jan 15; 517(7534): 360–364. Published online 2014 Oct 29. doi: 10.1038/nature13864

PMCID:: PMC4297598

Article PDF–1.5M

Select item 395405612.

FVIIa as used pharmacologically is not TF dependent in hemophilia B mice

Dengmin Feng, Herbert Whinna, Dougald Monroe, Darrel W. Stafford

Blood. 2014 Mar 13; 123(11): 1764–1766. Prepublished online 2014 Jan 14. doi: 10.1182/blood-2013-08-522987

PMCID:: PMC3954056

Article

Select item 395245413.

Prolonged half-life and preserved enzymatic properties of factor IX selectively PEGylated on native N-glycans in the activation peptide

Henrik Østergaard, Jais R. Bjelke, Lene Hansen, Lars Christian Petersen, Anette A. Pedersen, Torben Elm, Flemming Møller, Mette B. Hermit, Pernille K. Holm, Thomas N. Krogh, Jørn M. Petersen, Mirella Ezban, Brit B. Sørensen, Mette D. Andersen, Henrik Agersø, Haleh Ahmadian, Kristoffer W. Balling, Marie Louise S. Christiansen, Karin Knobe, Timothy C. Nichols, Søren E. Bjørn, Mikael Tranholm

Blood. 2011 Aug 25; 118(8): 2333–2341. Prepublished online 2011 Jun 23. doi: 10.1182/blood-2011-02-336172

PMCID:: PMC3952454

Article

Select item 382172414.

Robust ZFN-mediated genome editing in adult hemophilic mice

Xavier M. Anguela, Rajiv Sharma, Yannick Doyon, Jeffrey C. Miller, Hojun Li, Virginia Haurigot, Michelle E. Rohde, Sunnie Y. Wong, Robert J. Davidson, Shangzhen Zhou, Philip D. Gregory, Michael C. Holmes, Katherine A. High

Blood. 2013 Nov 7; 122(19): 3283–3287. Prepublished online 2013 Oct 1. doi: 10.1182/blood-2013-04-497354

PMCID:: PMC3821724

Article

Select item 295468215.

Intraarticular factor IX protein or gene replacement protects against development of hemophilic synovitis in the absence of circulating factor IX

Junjiang Sun, Narine Hakobyan, Leonard A. Valentino, Brian L. Feldman, R. Jude Samulski, Paul E. Monahan

Blood. 2008 Dec 1; 112(12): 4532–4541. Prepublished online 2008 Aug 20. doi: 10.1182/blood-2008-01-131417

PMCID:: PMC2954682

Article

Select item 293823416.

Factor IX ectopically expressed in platelets can be stored in α-granules and corrects the phenotype of hemophilia B mice

Guowei Zhang, Qizhen Shi, Scot A. Fahs, Erin L. Kuether, Christopher E. Walsh, Robert R. Montgomery

Blood. 2010 Aug 26; 116(8): 1235–1243. Prepublished online 2010 May 5. doi: 10.1182/blood-2009-11-255612

PMCID:: PMC2938234

Article

Select item 200050117.

A mouse model for nonsense mutation bypass therapy shows a dramatic multiday response to geneticin

Chunmei Yang, Jinong Feng, Wenjia Song, Jicheng Wang, Becky Tsai, Yunwu Zhang, William A. Scaringe, Kathleen A. Hill, Paris Margaritis, Katherine A. High, Steve S. Sommer

Proc Natl Acad Sci U S A. 2007 Sep 25; 104(39): 15394–15399. Published online 2007 Sep 19. doi: 10.1073/pnas.0610878104

PMCID:: PMC2000501

Article PDF–332K

Select item 963966018.

Liver-heart cross-talk mediated by coagulation factor XI protects against heart failure

Yang Cao, Yuchen Wang, Zhenqi Zhou, Calvin Pan, Ling Jiang, Zhiqiang Zhou, Yonghong Meng, Sarada Charugundla, Tao Li, Hooman Allayee, Marcus M. Seldin, Aldons J. Lusis

Science. Author manuscript; available in PMC 2022 Nov 7.

Published in final edited form as: Science. 2022 Sep 23; 377(6613): 1399–1406. Published online 2022 Sep 22. doi: 10.1126/science.abn0910

PMCID:: PMC9639660

Article PDF–1.9M

Select item 820067719.

Effect of CpG Depletion of Vector Genome on CD8⁺ T Cell Responses in AAV Gene Therapy

Thais B. Bertolini, Jamie L. Shirley, Irene Zolotukhin, Xin Li, Tsuneyasu Kaisho, Weidong Xiao, Sandeep R. P. Kumar, Roland W. Herzog

Front Immunol. 2021; 12: 672449. Published online 2021 May 31. doi: 10.3389/fimmu.2021.672449

PMCID:: PMC8200677

Article PDF–2.8M

Select item 781041220.

Evaluating the potential benefits of the extravascular pool of factor IX

David Lillicrap

Blood Coagul Fibrinolysis. 2021 Jan; 32(1): 68–69. Published online 2021 Nov 23. doi: 10.1097/MBC.0000000000000969

PMCID:: PMC7810412

Article PDF–72K

PMC

Result Filters

Article attributes

Text availability

Publication date

Custom date range

Research Funder

Additional filters

Display Settings:

Send to:

Links from Gene

Items: 1 to 20 of 48

Display Settings:

Send to:

Supplemental Content

Find related data

Recent activity